Fig. 1
From: Golodirsen restores DMD transcript imbalance in Duchenne Muscular Dystrophy patient muscle cells

Exon 53 skipping efficiency & transcript amount. A Graphical representation of exon skipping efficiency percentage (Y-axis) among patients (X-axis). Squares represent the mean exon skipping percentage for 3 technical replicates per sample ± SD. B Graphical representation of DMD transcript expression in treated cultures (black bars) normalised to non-treated cultures (white bars). Non-treated transcripts amount among samples are set as 1 to facilitate the graphical visualization. Transcript expression (Y-axis) is expressed as ratio between treated and non-treated cultures